Original Source(s)
Related Content
The drugs and devices have been on the market for years. But FDA-ordered studies still aren’t done.
“Doctors rely on this evidence, patients rely on this evidence, and if that evidence is not there, it’s going to lead to a lot of uncertainty."
September 22, 2026
-
14 min
Treatable Pediatric Neuromuscular Disorders
Through a case-based, evidence-driven approach, this Neuroscience Grand Rounds session highlights how clinicians can differentiate among neuromuscular conditions, localize disease processes and identify those disorders where timely treatment can significantly alter disease trajectory.
June 19, 2026
-
1 min
First MCT8 deficiency therapy approved
Clinical studies showed reductions in circulating thyroid hormone levels and changes in heart rate and systolic blood pressure.
September 29, 2026
-
3 min