Maternal-Fetal Administration of Risdiplam Partially Rescues the SMNΔ7 Mouse Model of Spinal Muscular Atrophy - Top-Institutions - MDSpire

Maternal and Fetal Delivery of Risdiplam Provides Partial Rescue in the SMNΔ7 Mouse Model of Spinal Muscular Atrophy

  • By

  • Emma R. Sutton

  • Ariane Beauvais

  • Rebecca Yaworski

  • Hugh J. McMillan

  • Rashmi Kothary

  • July 15, 2026

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Top Institutions in Neurology

Brief introduction explaining scope and methodology.

  • #1

    Ottawa Hospital Research Institute
    Ottawa Hospital Research Institute

    Ottawa, Ontario

    Key Differentiators

    • Neurology
    • Pediatrics
  • #2

    St. Jude Children’s Research Hospital
    St. Jude Children’s Research Hospital

    Memphis, Tennessee

    Key Differentiators

    • Pediatrics
    • Neurology
  • #3

    Children’s Hospital of Philadelphia
    Children’s Hospital of Philadelphia

    Philadelphia, Pennsylvania

    Key Differentiators

    • Pediatrics
    • Neurology

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